Cell & Gene - Resources

03/04/24 - Scarlet Therapeutics uses genetic manipulation of red blood cells to carry a higher load of therapeutic proteins to help treat rare metabolic diseases.

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Gene Therapy Development

Post-Event Proceedings – Gene Therapy Development & Manufacturing 2023

Concise and insightful summaries of presentations delivered by prominent thought leaders at Gene Therapy Development & Manufacturing 2023.

Gene Therapy Development

Curing HIV with cell & gene therapy?

It is now possible to live a long and near normal life with HIV, but what is the likelihood of a permanent cure?

Gene Therapy Development

Safety in Viral Vectors and Viral Clearance: Ensuring Efficacy and Security in Biopharmaceuticals

We discuss the challenges and safety measures in using viral vectors for gene therapies, focusing on vector selection, safety testing, quality control, and contamination prevention, highlighting their importance for the success of advanced medical treatments.

Gene Therapy Development

Viral Vectors in Molecular Biology and Gene Therapy

Adeno-associated viral (AAV) vectors dominate gene therapy due to their efficiency and safety, although challenges remain in addressing toxicity and expanding applications.

Gene Therapy Development

Innovation Hubs for Gene Therapies: Advancing the Academic-Led Clinical Development of Novel Gene Therapies

The UK's cell and gene therapy sector is on the threshold of becoming a global leader in the field. While present challenges include the supply of equipment and skills gaps, Innovation Hubs aim to bridge these through collaboration.

Gene Therapy Development

Replacing the EU's Clinical Trials Directive: A Sea Change in Clinical Trial Execution

The EU's Clinical Trials Regulation has replaced the union's former Clinical Trials Directive, introducing a centralised application process which aims to ensure consistent timelines for clinical trial reviews.

Gene Therapy Development

Tracking Fibonacci Spirals in Plant Evolution and Morphology

Examples of Fibonacci spirals in nature include monkey puzzle trees, the double helix of human DNA, and even certain atmospheric patterns. Now, a new study from the University of Edinburgh suggests that the presence of these patterns in early plants may not be as ubiquitous as previously thought.

Gene Therapy Development

Accelerate Your Cell and Gene Therapy Analytics

Gene Therapy Development

Biocair - Advanced Cold Chain Packaging Options

Gene Therapy Development

Biocair - Delivering Personalised Supply Chains for Autologous Cell Therapies

Gene Therapy Development

Biocair - Your Partner for Life Science Logistics

Gene Therapy Development

Ella - Precision Multiplexing Made Simple

Gene Therapy Development

Identifying Highly Potent TNF-Alpha Secreting T Cells from Blood Samples

Gene Therapy Development

Imaged cIEF, CE-SDS, and Imaged cIEF Fractionation

Gene Therapy Development

Localising Lentiviral Transduction-Inserted CAR Cassettes in T Cells Using Xdrop

Gene Therapy Development

Jess - Your Complete Protein Analysis Solution

Gene Therapy Development

Professional Assay Services Offers GCLP-Compliant RNAscope, BASEscope, and miRNAscope

Gene Therapy Development

Qualifying Individual Cells in a Cytokine Secretion Assay

Gene Therapy Development

Rapidly Identifying Active Natural Killer Cells Using an Xdrop Single-Cell Format Assay Based on Double-Emulsion Droplets

Gene Therapy Development

Revealing and Retrieving Highly Potent IFN-y Secretors Using an Xdrop Single-Cell Format Workflow

Gene Therapy Development

Simplifying Transgene Insertion Analysis with Xdrop Sort

Gene Therapy Development

Wilhelm Johannsen, Beans, and the Origins of Genotype and Phenotype

We spend a lot of time discussing new cell and gene therapies, as well as their implications for future treatment. But where did the term ‘gene' come from?

Gene Therapy Development

Approved Gene Therapy Products Brought to Market Through the use of AI

Many of the biggest roadblocks in gene therapy development can be removed by tapping into longitudinal datasets facilitated by AI techniques and machine learning, tracking the real-world progress of clinical trial participants.

Gene Therapy Development

CGT Manufacturing: Key Considerations for Implementing AI/ML Approaches

AI/ML approaches are not some miracle ‘one size fits all' fix-all for delays and holdups in CGT manufacture, but the proper implementation of deep learning approaches and data interpretation may help speed up development.

Gene Therapy Development

FDA Pursues Accelerated Approval Path Following Cell and Gene Therapy Backlog

The announcement comes with the news that the cell and gene therapy manufacturing market is now worth US$ 19.3 billion, with a compound annual growth rate (CAGR) of 29% between 2022 and 2023.

Gene Therapy Development

Fortunes Brighten for Bluebird Bio as Cash Runway Extended to 2024

After a rocky year, bluebird bio's approval journey for a treatment for sickle cell disease looks to be back on track, with the company generating more funds by selling shares.

Gene Therapy Development

Abundant Stochastic Off-Target Activity by Base Editors

Can complementary approaches for off-target quantification demonstrate substantial levels in various state-of-the-art editors?

Gene Therapy Development

When to Cut and When to Inhibit? A Low-Throughput, Hands-On Investigation Of CRISPR-Cut and CRISPRi Efficiencies In iPSC And Neural Cells

Gene knockdown – the manual reduction of a particular gene's expression in target cells – entails the modification of cellular development in young cells. CRISPR gene editing techniques enable researchers such as Pia Johansson to induce gene knockdown in target cells.

Gene Therapy Development

Overcoming the Challenges of Precision Genome Editing

Experts from academia and industry discuss the current obstacles and opportunities for genome editing during a roundtable session at Gene Therapy Development & Manufacturing: In-Person.

Gene Therapy Development

Refining Analytics for Gene Delivery Systems

Key opinion leaders from Roche and Purespring Therapeutics debate future strategies for advancing cell and gene therapeutics.

Gene Therapy Development

Daikyo Crystal Zenith® Case Study: Meeting the Challenge of Viral Vector Delivery

Gene Therapy Development

West Pharmaceutical Solutions: Protect Your Gene Therapy Product with an Approved Container Closure System

Gene Therapy Development

West Pharmaceutical Solutions: Packaging Containment Solutions for Gene Therapy Products

Gene Therapy Development

West Pharmaceutical Solutions: Gene Therapy and Daikyo Crystal Zenith® Vials Case Study

Gene Therapy Development

Inciting Rapid Standardisation in Cell and Gene Therapy Manufacturing

Can the cell and gene therapy field create industry consensus on a more detailed level? In this Insight Article, Jorgen Magnus, Strategic Program Lead of Cell and Gene Therapy at Bayer, highlights the promise of process mapping for reaching a harmonised approach to development and manufacturing standards.

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